14800-DvRappard

80 Chapter 5 Table 1 : Evolution with and without HCT Patient ID MLD type Follow-up since HCT (months) GMF pre HCT GMF post HCT* Cognition pre HCT (age in years/months) Cognition post HCT (age in years) MRI pre HCT MRI post HCT* Deceased (age in years) Transplanted patients MLD-50 Late-infantile 10 2 6 DQ 105 (25m) NA 2 20 yes (3y) MLD-45 Late-infantile 60 2 5 DQ 101 (35m) 70 (4y) 3 8 no MLD-16 Juvenile 36 0 0 104 (6y) NA 0 0 no MLD-37 Juvenile 127 0 2 DQ 116 (26m) 95 (6y) 2 4 no MLD-4 Juvenile 112 1 1 110 (5y) 56 (10y) 4 8 no MLD-53 Juvenile 11 1 6 74 (7y) NA 20 25 yes (8y) MLD-14 Juvenile 61 1 1 94 (14y) 93 (17y) 12 11 no MLD-21 Adult 27 0 0 100 (17y) 95 (18y) 10 10 no MLD-30 Adult 94 0 1 104 (19y) 107 (21y) 7 11 no MLD-41 Adult 77 0 0 91 (25y) 89 (27y) 12 13 no MLD-15 Adult 59 0 0 87 (35y) 73 (40y) 11 14 no MLD-51 Adult 2 1 2 61 (22y) NA 16 24 yes (22y) MLD-2 Adult 62 0 0 72 (28y) 76 (31y) 13 12 no

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