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84 Chapter 5 16. MartinHR,PoeMD,ProvenzaleJM,KurtzbergJ,MendizabalA,EscolarML.Neurodevelopmental outcomes of umbilical cord blood transplantation in metachromatic leukodystrophy. Biol Blood Marrow Transplant. 2013;19:616–624. 17. Sevin C, Aubourg P, Cartier N. Enzyme, cell and gene-based therapies for metachromatic leukodystrophy. J Inherit Metab Dis. 2007;30:175–183. 18. Cable C, Finkel RS, Lehky TJ et al. Unrelated umbilical cord blood transplant for juvenile metachromatic leukodystrophy: a 5-year follow-up in three affected siblings. Mol Genet Metab. 2011;102:207–209. 19. Krageloh-Mann I, Groeschel S, Kehrer C et al. Juvenile metachromatic leukodystrophy 10 years post transplant compared with a non-transplanted cohort. Bone Marrow Transplant. 2013;48:369-375.